Keyphrases
Dystrophin
72%
RNA Processing
48%
Dp71
48%
Alternative Splicing
35%
Duchenne
31%
Splicing Factor
24%
RNA-based Therapeutics
24%
Mutually Beneficial
24%
Human Cells
24%
Neurological Diseases
24%
Cambridge
24%
Northampton
24%
Duchenne muscular Dystrophy
18%
Exon
11%
Targeted Treatment
8%
Brain Targeting
8%
In Vitro Splicing Assay
8%
Western Blotting
8%
Resubmission
8%
Specific Intent
8%
Quantitative PCR
8%
Quality of Life
6%
Muscle Protein
6%
Knowledge Gaps
6%
Rare Genetic Disease
6%
Accelerated Development
6%
RNA-RNA
6%
RNA Aptamer
6%
RNA-based Therapy
6%
Untapped Potential
6%
Safe Delivery
6%
Therapeutic Landscapes
6%
Small Interfering RNA (siRNA)
6%
Rapid Progress
6%
Antisense Oligonucleotides
6%
Neurology
6%
Behavioral Disorders
6%
Central Nervous System Tumors
6%
Alzheimer's Disease
6%
Neurodegenerative Diseases
6%
Ischemic Stroke
6%
Efficient Delivery
6%
Cognitive Impairment
5%
Intellectual Disability
5%
Genetic Disease
5%
INIS
brain
100%
rna processing
48%
splicing
48%
proteins
29%
rna
27%
modeling
26%
precision
24%
regulations
24%
diseases
24%
muscles
17%
exons
12%
universities
12%
drugs
10%
losses
10%
feedback
8%
in vitro
8%
proposals
8%
pcr
8%
patients
7%
genetics
7%
quality of life
5%
applications
5%
central nervous system
5%